orphan drug

基本解释

Objective: To introduce American Orphan Drug System.
目的：介绍美国罕见病药物制度。
A drug is eligible for orphan drug designation if it is intended to treat a disease or condition that affects less than 200,000 people in the United States.
当一种疾病影响小于20万美国人时，治疗该疾病的药品被指定为稀少药品。
Orphan drug designation is available for drugs already approved for another disease or condition or for experimental drugs that have not been previously approved.
已经被批准用于其它疾病治疗的药物或者是尚处于试验阶段未被批准的药物都可以通过孤儿药物申报程序进行。

Without the Orphan Drug Act, there would probably be no Biogen Idec, no Genzyme, Alexion Pharmaceuticals.
FORBES: How The Odd Couple's Jack Klugman Helped Create The Biotech Industry
One idea is to create an incentive for drugmakers comparable to that in the Orphan Drug Act.
FORBES: Magazine Article
AZT, began as an orphan drug for what was then an obscure disease of the immune system.
ECONOMIST: Rare diseases: Safety in numbers